Study Of The Long-Term Safety Of Vamorolone In Patients With Duchenne Muscular Dystrophy
Seeking boys aged 2 and older with Duchenne Muscular Dystrophy who have been prescribed Vamorolone (Agamree) for a study of the long-term safety of the drug.
7 Studies found
Bone Joint and Muscle Diseases
Bone Joint and Muscle Diseases
Study Of An Investigational Drug For Boys With Duchene Muscular Dystrophy
Seeking boys aged 6-14 years old who have previously been treated with adeno-associated virus (AAV) based gene therapy for a study of an investigational drug
Bone Joint and Muscle Diseases
Study Of An Investigational Drug To Preserve Muscle Function In Boys With Duchenne Muscular Dystrophy
Seeking boys aged 4 to 16 for a study of an investigational drug to increase dystrophin protein levels in muscles.
Bone Joint and Muscle Diseases
Duchenne Muscular Dystrophy (Dmd) And Becker Muscular Dystrophy (Bmd) Biorepository
Seeking boys and men with Duchenne muscular dystrophy (DMD) or Becker Muscular Dystrophy (BMD) to provide samples including blood, plasma, serum, urine, as well as the remainders of tissue samples collected as part of their usual clinical care for a biorepository.
Bone Joint and Muscle Diseases
Imaging Study Of Individuals Diagnosed With Duchenne Muscular Dystrophy (Dmd)
Seeking male participants aged 10-21 years of age who have been diagnosed with Duchenne Muscular Dystrophy (DMD) for participation in an imaging study.
Bone Joint and Muscle Diseases
Data Collection Study For Patients With Duchenne Muscular Dystrophy
This study is intended to collect data from medical records on patients who have Duchenne Muscular Dystrophy
Pediatrics
Study Of An Investigational Drug For Duchenne Muscular Dystrophy
Seeking boys aged 4-9 with Duchenne Muscular Dystrophy for a study of an investigational drug to prevent muscle damage.