Seeking boys aged 4-9 with Duchenne Muscular Dystrophy for a study of an investigational drug to prevent muscle damage.
Participants in this study will either get one of three different doses of the investigational drug or a placebo (looks like the investigational drug but contains no medicine) for 12 weeks. After the 12 week period there is a 40-week open-label extension where all participants can be on the investigational drug.
What we're hoping for
We are studying an investigational drug to prevent muscle damage in boys aged 4-9 with Duchenne Muscular Dystrophy.
ClinicalTrials.gov Identifier: NCT05540860