Seeking children aged 6 months and older with Tay-Sachs or Sandhoff disease for a study of the safety of an experimental gene therapy and whether it improves their ability to move.
Seeking men and women who have been hospitalized with COVID-19 for a study that compares the safety and activity of experimental regimens consisting of oral anti-inflammatory agents plus Remdesivir.
Adult male and female U.S. recipients of allogeneic or autologous HSC transplants or cellular therapies are eligible to participate in the NMDP Research Sample Repository.
Men and women over 16 years old undergoing transplantation with unlicensed CBUs (cord blood units) will be enrolled. Cord blood units not meeting FDA requirements or not yet approved by the FDA may be used for transplant if the transplant is done as part of a study.
Seeking adult men & women whose tumor cells have a change in a gene called ALK that causes the cells to grow and spread.