Seeking men and women aged 18-65 with Facioscapulohumeral Muscular Dystrophy (FSHD) for a study of an investigational drug to reduce the presence of DUX4 to prevent muscle cells from dying.
Participants in this study will be randomly assigned to get either the investigational drug or a placebo (looks like the drug but contains no medicine).
What we're hoping for
We are studying whether the investigational drug is safe and effective in reducing the protein DUX4 and slowing the progression of Facioscapulohumeral Muscular Dystrophy (FSHD)
ClinicalTrials.gov Identifier: NCT05397470