Conquering Diseases

Study Of An Investigational Drug For Facioscapulohumeral Muscular Dystrophy

Description

Seeking men and women aged 18-65 with Facioscapulohumeral Muscular Dystrophy (FSHD) for a study of an investigational drug to reduce the presence of DUX4 to prevent muscle cells from dying.

Overview

Participants in this study will be randomly assigned to get either the investigational drug or a placebo (looks like the drug but contains no medicine).

What we're hoping for

We are studying whether the investigational drug is safe and effective in reducing the protein DUX4 and slowing the progression of Facioscapulohumeral Muscular Dystrophy (FSHD)

Additional Information

ClinicalTrials.gov Identifier: NCT05397470

 Principal Investigator

Lawrence  Hayward, MD, PhD

University of Massachusetts Medical School

 Study Contact

Catherine  Douthwright

508-856-6491

Catherine.Douthwright@umassmed.edu

 Location

UMMS University Campus

55 Lake Ave North 

Worcester,MA 01655

508-856-8989