Conquering Diseases

Study Of An Investigational Drug For Duchenne Muscular Dystrophy


Seeking boys between the ages of 8 and 16 with Duchenne Muscular Dystrophy who are unable to walk 10 meters in 10 seconds for a study of an investigational drug.


Participants in this study will be randomly assigned to either receive the investigational drug or a placebo (looks like the drug, but contains no medicine) for 3 months followed by a 3 month period where all participants will take the investigational drug.

What we're hoping for

We hope to evaluate whether an investigational drug is safe and effective to improve muscle function in boys with Duchenne Muscular Dystrophy.

Additional Information Identifier: NCT04184882

 Principal Investigator

Brenda  Wong, MD

UMass Memorial Health Care

 Study Contact

Sarah  Figueira



UMMS University Campus

55 Lake Ave North 

Worcester,MA 01655